Amicus Therapeutics is a biopharmaceutical company that is run by Chairman and Chief Executive Officer John F. Crowley. Crowley’s children were both diagnosed with Pompe disease a rare neuromuscular disorder. Driven to create a cure for his children he delved into biotechnology without looking back. He was a father with a mission to save his kids, and that passion still drives the Amicus Therapeutics work ethic (Twitter). You can read more about John F. Crowley in “The Cure: How a Father Raised $100 Million-And Bucked the Medical Establishment-In a Quest to Save His Children” by Pulitzer Prize winning journalist Geeta Anand as well as his book “Chasing Miracles: The Crowley Family Journey of Strength, Hope, and Joy” (https://finance.yahoo.com/quote/FOLD?ltr=1) Amicus Therapeutics deals in biopharmaceutical which is a biological medical product used to treat a range of devastatingly rare diseases. One of their main biopharmaceutical products is Migalastat. Migalastat is used to treat patients with Fabry disease. Fabry is an X-linked disease with mutations in the GLA gene. Mutations in this cause alpha-Gal A, to be deficient or altogether absent. They create many others including ATB200/AT2221 a Pompe disease enzyme replacement therapy. Pompe disease is a Lysosomal Storage Disorder that is caused by a deficient amount of the enzyme acid alpha-glucosidase. Amicus Therapeutics has many different programs that are all geared toward rare and orphaned diseases, and their mission statement is simply to fight. It is a company that is driven to create a cure. They have many supporters including the Michael J. Fox Organization which donated a $500,000 grant for the furtherment of their practice and assisting David Geffen School of Medicine at the University of California, Los Angeles. Amicus Therapeutics will not stop. Their mission statement even reads, “We seek to deliver the highest quality therapies for persons living with these diseases.” Using the power of their minds and thinking differently the staff is passionate about what they do and what they do is save lives.